Chemical formula: C₃₆₄H₅₆₉N₁₇₇O₁₂₂P₃₀
Eteplirsen is designed to bind to exon 51 of dystrophin pre-mRNA, resulting in exclusion of this exon during mRNA processing in patients with genetic mutations that are amenable to exon 51 skipping.
This medicinal substance has been classified in the anatomical therapeutic chemical (ATC) classification according to its main therapeutic use as follows:
| ATC code | Group title | Classification |
|---|---|---|
| M09AX06 | M Musculo-skeletal system → M09 Other drugs for disorders of the musculo-skeletal system → M09A Other drugs for disorders of the musculo-skeletal system → M09AX Other drugs for disorders of the musculo-skeletal system | |
Competent medicine agencies globally have authorized commercialization of this active ingredient according to these medication package inserts (MPIs):
| Title | Information Source | Document Type | |
|---|---|---|---|
| EXONDYS 51 Solution for injection | FDA, National Drug Code (US) | MPI, US: SPL/PLR |
Eteplirsen is an active ingredient of these brands:
United States (US)Israel (IL)Note the following: The list of brand names is continuously updated, and thus does not include the total of products circulating worldwide. |
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